2nd Rare Disease Innovation Summit

June 12, 2019 – June 13, 2019  • Boston, MA

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Science Spotlight – Advancements in Gene Therapy that are Tearing Down Barriers to Discovery in Rare Disease . Regulatory Update – Program Updates and New Initiatives within the FDAʼs Orphan Drug Program. Technology Showcase – How A.I. and Advanced Data Analytics are Reshaping Complex Diagnostics and Decision-Making. Patient Perspectives – Cures, Community Collaboration and the Care Continuum for Patients and Caregivers. Funding Focus – The Impact of Disruptive Investors and Insight on What Investors Look For and Financial Models for Success