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World Orphan Drug Congress USA 2018

April 25, 2018 – April 28, 2018  • Gaylord National Harbor Hotel Oxon Hill, Maryland

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The 8th annual World Orphan Drug Congress USA will be held on April 25-27, 2018 at the Gaylord National Harbor Hotel in Oxon Hill, Maryland. 

Join 800+ leaders in orphan drugs from 50 countries, covering all aspects of orphan drug development and rare disease research.

For 2018, we’re moving to a stellar venue – the Gaylord National Resort & Convention Center – right outside of Washington D.C. With 12 seminars and workshops on the pre-conference day, and a full 6-stream program including orphan drugs tracks on Regulatory, Clinical & Access Innovation; Commercialization; Global Market Access; Genetics & Diagnostics; as well as Rare Disease Advocacy World and Pitch & Partner, this is set to be the largest and most comprehensive orphan drugs conference in the world.


Speakers include:

  • Yann Le Cam, Chief Executive Officer, EURORDIS 

  • Jacqueline Corrigan-Curay, Director, Office of Medical Policy, Center for Drug Evaluation and Research, FDA

  • Tim Miller, Chief Executive Officer, Abeona Therapeutics

  • Mark Rothera, Chief Executive Officer, Orchard Therapeutics 

  • Amrit Ray, Senior Vice President, Science & Medicine, Johnson & Johnson

  • Sandy Macrae, President and Chief Executive Officer, Sangamo Therapeutics

  • Katrine Bosley, Chief Executive Officer, Editas Medicine 

  • Rodger Novak, Chief Executive Officer and Founder, CRISPR Therapeutics 

  • Makoto Suematsu, President, Japan Agency for Medical Research and Development

  • Rick Chapman, Director of Health Economics, ICER

  • Nessan Bermingham, Chief Executive Officer, President and Founder, Intellia Therapeutics 

  • Catherine Stehman-Breen, Senior Vice President and Chief Medical Officer, Sarepta Therapeutics

  • Ron Bartek, President, Friedreich's Ataxia Research Alliance (FARA)

  • Diane Kleinermans, Advisor to the Ministry of Health and Social Affairs, Belgium Ministry of Public Health and Social Security

  • Edmund Jessop, Medical Advisor, NHS England

  • Preston Campbell, President, Cystic Fibrosis Foundation

For more information & to register, visit www.terrapinn.com/WODCUSA18